The Zebras Herd
The Zebras Herd, the Home of Ultrarare, is the podcast of the RTW Foundation. Here you will find topical conversations with people interested in developing therapies for ultrarare diseases.
RTW Foundation – Advancing rare disease research (rtwcf.org)
The Zebras Herd
Episode 3. Timothy Yu
April 30, 2024
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RTW Charitable Foundation
Tim Yu is a neurologist at Boston Children’s Hospital. He is responsible for one of the first examples of individualized genetic medicine – the drug milasen. In this episode, we spoke about his approach to drug development, about how he engages with ultrarare patients, about his thoughts on equity, and about the impact of the N=1 Collaborative.